Pharmacoeconomic review report Nitisinone (Orfadin) (Sobi Canada Inc.)
Nitisinone (Orfadin) is indicated for the treatment of patients with hereditary tyrosinemia type 1 (HT- 1) in combination with dietary restriction of tyrosine and phenylalanine. Nitisinone is available as 2 mg, 5 mg, 10 mg, and 20 mg capsules for oral administration. The submitted price of nitisinon...
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Autor Corporativo: | |
Formato: | Libro electrónico |
Idioma: | Inglés |
Publicado: |
Ottawa (ON) :
CADTH
2018.
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Materias: | |
Ver en Biblioteca Universitat Ramon Llull: | https://discovery.url.edu/permalink/34CSUC_URL/1im36ta/alma991009820268806719 |
Tabla de Contenidos:
- Abbreviations
- Executive Summary
- Information on the Pharmacoeconomic Submission
- Summary of the Manufacturer's Pharmacoeconomic Submission
- Manufacturer's Base Case
- Summary of Manufacturer's Sensitivity Analyses
- Limitations of Manufacturer's Submission
- CADTH Common Drug Review Reanalyses
- Issues for Consideration
- Patient Input
- Conclusions
- Appendix 1. Cost Comparison
- Appendix 2. Summary of Key Outcomes
- Appendix 3. Additional Information
- Appendix 4. Summary of Other Health Technology Assessment Reviews of Drug
- Appendix 5. Reviewer Worksheets
- References.