Pharmacoeconomic review report Sapropterin dihydrochloride (Kuvan)
Sapropterin (SAP) (Kuvan) is indicated in conjunction with a phenylalanine (Phe)-restricted diet to reduce blood Phe levels in patients with hyperphenylalaninemia (HPA) due to tetrahydrobiopterin (BH4)-responsive phenylketonuria (PKU). The initial dosage is 20 mg/kg/day administered orally for a per...
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Formato: | Libro electrónico |
Idioma: | Inglés |
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Ottawa (ON) :
Canadian Agency for Drugs and Technologies in Health
2017.
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Colección: | Common drug review clinical review report.
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Ver en Biblioteca Universitat Ramon Llull: | https://discovery.url.edu/permalink/34CSUC_URL/1im36ta/alma991009820268106719 |