Advancing gene-targeted therapies for central nervous system disorders proceedings of a workshop

"On April 23 and 24, 2019 the Forum on Neuroscience and Nervous System Disorders convened a workshop titled "Advancing Gene-Targeted Therapies for Central Nervous System Disorders" in Washington, DC. This public workshop brought together experts and key stakeholders from academia, gov...

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Detalles Bibliográficos
Autor principal: National Academies of Sciences, Engineering, and Medicine (-)
Autores Corporativos: National Academies of Sciences, Engineering, and Medicine (U.S.). Health and Medicine Division, contributor (contributor), National Academies of Sciences, Engineering, and Medicine (U.S.). Board on Health Sciences Policy, contributor, National Academies of Sciences, Engineering, and Medicine (U.S.). Forum on Neuroscience and Nervous System Disorders, contributor
Otros Autores: Bain, Lisa J. contributor (contributor), Stroud, Clare, contributor
Formato: Libro electrónico
Idioma:Inglés
Publicado: Washington, District of Columbia : The National Academies Press [2019]
Materias:
Ver en Biblioteca Universitat Ramon Llull:https://discovery.url.edu/permalink/34CSUC_URL/1im36ta/alma991009621946906719
Tabla de Contenidos:
  • Introduction and overview
  • Exploring the current landscape of central nervous system gene-targeted therapies
  • Gene-targeted therapy approaches for central nervous system disorders : opportunities and challenges
  • Translating gene-targeted therapies from bench to bedside
  • Meaningful engagement of patients and families
  • Future directions in the development of gene-targeted therapies
  • Appendixes